Watch the highlights of Gavriel Rosenfeld in conversation with Dr Ronni Cohn at our virtual event: An Evening with the Duchenne Research Fund. More than 400 people tuned in to hear Gavriel talk about living with Duchenne, mental health, juggling school and hospital visits, and more.
DRF co-founders Kerry & Doron Rosenfeld welcomed viewers from across five continents who came together to learn more about the DRF’s most recent achievements and the challenges Covid has presented for the Duchenne arena.
Dr Cohn, who is also Chair of the DRF’s Scientific Advisory Board, paid tribute to its dedicated supporters, saying that DRF’s seed funding of Solid Biosciences’ gene therapy program had been enabled by the support of all the donors, and created momentum and investor appetite for Duchenne muscular dystrophy research.
“I think it’s fair to say that the initial support of the DRF to Solid’s gene therapy program was the catalyst that the field needed to finally move gene therapy to the clinical stage,” he said, citing that there are now four gene therapy clinical trials ongoing for Duchenne, with a fifth likely to start soon.
Watch the full one-hour event
The full event can also be viewed below. We are extremely grateful to Dr Joel Schneider, CTO of Solid Biosciences; Dr Barry Byrne, Associate Chair of Paediatrics at the University of Florida; and Great Ormond Street Hospital Senior Research Physiotherapist Victoria Selby, who presented research updates during the event.