Gene therapy for Becker

Gene therapy for Becker A microdystrophin gene therapy approach for Becker muscular dystrophy We have awarded a grant to the team of Professor Thomas Voit (pictured) at the Great Ormond Street Biomedical Research Centre at UCL to develop a microdystrophin gene therapy...

Solid GT

Solid GT Ground-breaking gene therapy platform for Duchenne (IGNITE DMD Clinical Trial) In 2014 we combined with Duchenne UK (previously Duchenne Children’s Trust) and Joining Jack to jointly invest $5 million into Solid Biosciences, a US-based disease-focused biotech...