Solid begins dosing patients in new gene therapy study

Inspire Duchenne study under way at two US sites

DMD Care UK launches new respiratory guidance

New guidance approved by British Thoracic Society

Vamorolone approved in the UK

DRF-funded treatment approved for patients aged 4 and over

Exploring next steps for patient care

DMD Care UK national meeting held on Rare Disease Day 2024

DRF highlights psychosocial research

Dozens of families attended DUK’s latest parent information day

Dedicated mental health support put in place for Duchenne families

DRF-funded programme has appointed two psychiatrists and a psychologist to tackle lack of support

£6m raised for Duchenne research

Cutting edge research in clinical trial thanks to your generosity.

Finding a cure for Duchenne

We accelerate treatments for Duchenne muscular dystrophy, the biggest genetic killer of children worldwide

Solid begins dosing patients in new gene therapy study

Inspire Duchenne study under way at two US sites

DMD Care UK launches respiratory guidance

Approved by the British Thoracic Society

Vamorolone approved in the UK

DRF-funded treatment approved for patients aged 4 and over

Exploring next steps for patient care

DMD Care UK national meeting held on Rare Disease Day 2024

DRF highlights psychosocial research

Dozens of families attended DUK’s latest parent information day

Dedicated mental health support put in place for Duchenne families

DRF-funded programme has appointed two psychiatrists and a psychologist to tackle lack of support

£6m raised for Duchenne research

Cutting edge research is in clinical trial thanks to your generosity.

Finding a cure for Duchenne

We accelerate treatments for Duchenne muscular dystrophy:
the biggest genetic killer of children worldwide

MILLION pounds raised thanks to our dedicated supporters

projects funded to help combat the biggest genetic killer of children

other patient organisations with which we have proudly collaborated

Our mission

We aim to stop Duchenne muscular dystrophy being a death sentence for hundreds of thousands of boys worldwide.

Our impact

We are helping turn the hope of treatments into reality. Critical treatments are in clinical trial thanks to our funds.

Your help

Your generosity has funded millions of pounds worth of  ground-breaking research. And there is still work to do.