Run the London Marathon with DRF

We have a few places left in #TeamDRF. Click below to find out more.

Covid-19 update

In line with government guidance we are continuing our work remotely. Please get in touch if you intend to send any donations by post, or alternatively please donate online. We are so grateful for your continued support – please stay safe.

ReveraGen receives $3.3m NIH grant

Award will help fund new drug application (NDA) for steroid alternative treatment for Duchenne.

Solid partners with Ultragenyx

Collaboration will focus on development and commercialisation of new gene therapies for Duchenne.

Sensor study extended into 2021

DRF-funded KineDMD study at Imperial and Great Ormond Street is now recruiting more patients.

£6m raised for Duchenne research

Cutting edge research is now in clinical trial thanks to our funds.

Finding a cure for Duchenne

We accelerate treatments for Duchenne muscular dystrophy: 
the biggest genetic killer of children worldwide

Run the London Marathon with DRF

We have a few places left in #TeamDRF. Click below to find out more.

Covid-19 update

In line with government guidance we are continuing our work remotely. Please get in touch if you intend to send any donations by post, or alternatively please donate online. We are so grateful for your continued support – please stay safe.

ReveraGen receives $3.3m NIH grant

Award will help fund new drug application for Vamorolone for Duchenne.

Solid partners with Ultragenyx

Collaboration will focus on development and commercialisation of new gene therapies for Duchenne.

Sensor study extended into 2021

DRF-funded KineDMD study at Imperial and Great Ormond Street recruiting more patients.

£6m raised for Duchenne research

Cutting edge research is now in clinical trial thanks to our funds.

Finding a cure for Duchenne

We accelerate treatments for Duchenne muscular dystrophy:
the biggest genetic killer of children worldwide

MILLION pounds raised thanks to our dedicated supporters

projects funded to help combat the biggest genetic killer of children

other patient organisations with which we have proudly collaborated

Our mission

We aim to stop Duchenne muscular dystrophy being a death sentence for hundreds of thousands of boys worldwide.

Our impact

We are helping turn the hope of treatments into reality. Critical treatments are in clinical trial thanks to our funds.

Your help

In the last 4 years we have given more than £3m to ground-breaking research projects.
And there is still work to do.