Neurobehavioural issues in Duchenne

Neurobehavioural issues in Duchenne Tackling learning, behaviour, depression and anxiety Although the physical challenges of Duchenne have been investigated extensively, the neurobehavioural and psychosocial issues that can result from the diagnosis are...

GOSH Physiotherapist

Great Ormond Street Hospital Senior Physiotherapist Nicola Burnett Children with Duchenne lose ambulation (the ability to walk) around their early teens. During this time and beyond, physiotherapy and focus on upper body strength are vital for non-ambulant patients to...

Non-viral delivery

Non-viral delivery for gene therapy A next generation gene therapy delivery approach The Duchenne Research Fund has committed £640,000 to accelerate research into alternative ways to deliver gene therapy to Duchenne patients, with the aim of increasing the number of...

CRISPR

CRISPR for Duchenne Genome editing technology to correct the mutated dystrophin gene The Duchenne Research Fund has awarded a £200,000 grant to the team at the Hospital for Sick Children in Toronto, Canada (‘Sick Kids’), who are working on using...

GOSH coordinator

Great Ormond Street Hospital Clinical Trial Co-ordinator Manju Agarwal As part of the Newcastle Plan in 2015/16, eight patient organisations contributed £1.2m to fund at least 16 vital posts across the UK to support and expand clinical trial capacity for Duchenne...