Combating immunity

Combating immunity to AAV Ensuring as many patients as possible can benefit from gene therapy The Duchenne Research Fund has awarded a grant to Dr Barry Byrne and Dr Manuela Corti’s team at the University of Florida, whose vital work focuses on overcoming...

Non-viral delivery

Non-viral delivery for gene therapy A next generation gene therapy delivery approach The Duchenne Research Fund committed £320,000 to accelerate research into alternative ways to deliver gene therapy to Duchenne patients, with the aim of increasing the number of...

Gene therapy for Becker

Gene therapy for Becker A microdystrophin gene therapy approach for Becker muscular dystrophy The Duchenne Research Fund has awarded a grant to the team of Professor Thomas Voit (pictured) at the Great Ormond Street Biomedical Research Centre at UCL to develop a...

Solid GT

Solid GT Ground-breaking gene therapy platform for Duchenne (IGNITE DMD Clinical Trial) The Duchenne Research Fund is proud to have funded one of the first gene therapy research programmes for Duchenne muscular dystrophy, which led to the IGNITE DMD Phase I/II...