Blood-based biomarker

Blood-based biomarker Developing a more informative measure of disease progression and response to new treatments Although Duchenne has been studied for many years, classic measures of disease progression rely on basic observations of movement, such as the six-minute...

Non-invasive imaging biomarker

Non-invasive imaging biomarker Reducing biopsies and improving dystrophin analysis Biopsies have become a difficult necessity for Duchenne patients who are involved in clinical trials. In addition to the stress on patients, each muscle can present disease differently,...

LTBP4

LTBP4 Targeting muscle inflammation and fibrosis With the funds raised in 2016, the DRF is tackling inflammation and fibrosis, which are two key problems for Duchenne boys. It is believed that the protein LTBP4 prevents the activation of a key biological pathway...

Treat-NMD Co-ordinator

Treat-NMD Duchenne Muscular Dystrophy Programme Co-ordinator Cathy Turner The Duchenne Research fund together with Duchenne UK and Joining Jack are jointly funding the Treat-NMD programme coordinator post for Duchenne at the John Walton Muscular Dystrophy Research...

Newcastle Senior Clinical Lecturer and Neurologist

Newcastle Senior Clinical Lecturer and Neurologist Dr Michela Guglieri The Duchenne Research Fund and six other leading Duchenne charities have jointly awarded a fellowship to Dr Michela Guglieri, a Senior Clinical Lecturer and Consultant Neurologist at Newcastle...