We are pleased to share a report from Great Ormond Street Hospital (GOSH) about the positive impact of the clinical staff posts that we helped to fund at the hospital as part of the DMD Hub, together with Duchenne UK, Harrison’s Fund and the Great Ormond Street Charity.
The report highlights that the charities’ funds have provided Professor Franceso Muntoni’s neuromuscular research team with the resources they needed to develop, expand and stabilise.
Since the funding was agreed, the number of patients recruited into trials has increased from 139 in 2016/17 to 351 in 2017/18.
In addition, at least 10 new commercial studies have commenced in that time.
The report says:
‘Associated improvements in the organisational, training and administrative process of clinical trials conducted by the team has led to an improved patient and family experience – assessments take less time, waiting times are minimised and there are fewer cancellations. The improvements in the team have also given the team the capacity to support and coordinate multicentre trials for potential new therapies, maximising access to these treatments.’