DRF Patron Evening

We hope you can join us on Thursday 20th June

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    Recent news

    Catch up on the latest developments in the projects we fund.

    DMD Care UK explores next steps for patient care

    On 29th February, Rare Disease Day, we were pleased to be part of the 2024 national meeting for DMD Care UK. More than 130 clinicians and 25 patient representatives are now involved in DMD Care UK …

    Vamorolone approved in the US

    The US FDA has approved Vamorolone for the treatment of Duchenne muscular dystrophy in children and adults aged 2 and over. It will be sold under the brand name Agamree …

    Our mission

    We aim to stop Duchenne muscular dystrophy being a death sentence for hundreds of thousands of boys worldwide.

    Our impact

    We are helping turn the hope of treatments into reality. Critical supportive drugs are in clinical trial thanks to our funds.

    Your help

    In the last 3 years we have given more than £1.5m to ground-breaking research projects.
    And there is still work to do.