Our projects

Brilliant scientists, powerful collaborations. We find and fund projects that are ripe for treating Duchenne now.

Biomarker research

Activity monitoring biomarker

Wearable sensor technology for Duchenne patients to monitor and analyse their daily activities.

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Non-invasive imaging biomarker

Reducing biopsies and improving dystrophin analysis in Duchenne boys.

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Blood-based biomarker

Measuring disease progression and response to new treatments.

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Pre-clinical research

LTBP4

Modifying the protein LTBP4 to target inflammation and fibrosis – two key challenges in Duchenne.

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Solid GT

A ground-breaking programme for exploring gene therapy for Duchenne.

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Vamorolone

An alternative to existing steroid treatments for Duchenne.

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Grants to support clinical and research staff and facilities

Dr Michela Guglieri

Newcastle Clinical Research Fellow

Cathy Turner

Treat-NMD Duchenne Programme Co-ordinator

Refurbishment and expansion of paediatric space

Clinical Research Facility at Newcastle Royal Infirmary

Awards for up-and-coming researchers

Kathy Wang

HHMI Medical Research Fellowship

Dr Patricia Piñol Jurado

World Muscle Society Congress prize

Some of our past projects

Ringo

Dystrophic dogs provide insights into Duchenne research.

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HT-100

Pre-clinical research for drug to target muscle fibrosis.

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SMT C1100

Increasing utrophin to compensate for dystrophin.

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Our commitment

We are passionate about supporting the most promising research to find therapies and a cure for Duchenne muscular dystrophy. We aim to focus our efforts on tackling Duchenne for all sufferers, regardless of their type of mutation. We have an open grant call and all applications are peer reviewed.

Our scientific advisory board comprises leading minds in the field: Professor Ronald Cohn, Dr Kevin Campbell, Professor Madeleine Durbeej-Hjalt and Dr James Dowling together with our Honorary Scientific Patron Professor Victor Dubowitz. Read more about their work here. Please contact research [at] duchenne.org.uk for more information about applications.

Our mission

We aim to stop Duchenne muscular dystrophy being a death sentence for hundreds of thousands of boys worldwide.

About us

Our impact

We are helping turn the hope of treatments into reality. Critical supportive drugs are in clinical trial thanks to our funds.

Latest news

Your help

In the last 3 years we have given more than £2m to ground-breaking research projects.
And there is still work to do.

Donate now